Hematopoietic Stem-Cell Gene Therapy for Cystinosis


KÜÇÜK H.

The New England journal of medicine, vol.394, no.20, pp.2064-2065, 2026 (SCI-Expanded, Scopus)

  • Publication Type: Article / Letter
  • Volume: 394 Issue: 20
  • Publication Date: 2026
  • Doi Number: 10.1056/nejmc2603539
  • Journal Name: The New England journal of medicine
  • Journal Indexes: Science Citation Index Expanded (SCI-EXPANDED), Scopus, Abstracts in Social Gerontology, BIOSIS, CINAHL, Educational research abstracts (ERA), EMBASE, Gender Studies Database, MEDLINE, MLA - Modern Language Association Database, Public Affairs Index, MLA International Bibliography, Academic Search Ultimate (EBSCO), Natural Science Collection (ProQuest), Biological Science Database (ProQuest), Health Research Premium Collection (ProQuest), Pharma Collection (ProQuest), Sociology Source Ultimate (EBSCO)
  • Page Numbers: pp.2064-2065
  • Gazi University Affiliated: Yes