A phase 1/2 study on intracerebroventricular tralesinidase alfa in patients with Sanfilippo syndrome type B.

Muschol N., Koehn A., Von Cossel K., Okur İ., Ezgu F. S., Harmatz P., ...Daha Fazla

The Journal of clinical investigation, cilt.133, 2023 (SCI-Expanded, Scopus)

  • Yayın Türü: Makale / Tam Makale
  • Cilt numarası: 133
  • Basım Tarihi: 2023
  • Doi Numarası: 10.1172/jci165076
  • Dergi Adı: The Journal of clinical investigation
  • Derginin Tarandığı İndeksler: Science Citation Index Expanded (SCI-EXPANDED), Scopus, Academic Search Premier, BIOSIS, CAB Abstracts, CINAHL, EMBASE, International Pharmaceutical Abstracts, MEDLINE, Veterinary Science Database, Directory of Open Access Journals
  • Gazi Üniversitesi Adresli: Evet