A phase 1/2 study on intracerebroventricular tralesinidase alfa in patients with Sanfilippo syndrome type B.

Muschol N., Koehn A., Von Cossel K., Okur İ., Ezgu F. S., Harmatz P., ...More

The Journal of clinical investigation, vol.133, 2023 (SCI-Expanded) identifier identifier identifier

  • Publication Type: Article / Article
  • Volume: 133
  • Publication Date: 2023
  • Doi Number: 10.1172/jci165076
  • Journal Name: The Journal of clinical investigation
  • Journal Indexes: Science Citation Index Expanded (SCI-EXPANDED), Scopus, Academic Search Premier, BIOSIS, CAB Abstracts, CINAHL, EMBASE, International Pharmaceutical Abstracts, MEDLINE, Veterinary Science Database, Directory of Open Access Journals
  • Gazi University Affiliated: Yes