Results of a Global Phase 3, Randomized, Double-Blind, Placebo-Controlled Trial Evaluating the Efficacy and Safety of Sebelipase Alfa as an Enzyme Replacement Therapy in Children and Adults with Lysosomal Acid Lipase Deficiency

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Balwani M., Burton B., Baric I., Bialer M., Burrow T. A., Camarena Grande C., ...Daha Fazla

HEPATOLOGY, cilt.60, sa.6, 2014 (SCI-Expanded, Scopus)

• Yayın Türü: Makale / Özet
• Cilt numarası: 60 Sayı: 6
• Basım Tarihi: 2014
• Dergi Adı: HEPATOLOGY
• Derginin Tarandığı İndeksler: Science Citation Index Expanded (SCI-EXPANDED), Scopus
• Gazi Üniversitesi Adresli: Evet