Safety and tolerability of SOBI003 in pediatric MPS IIIA patients key study design features of the ongoing first-in-human study


Broijersen A., Dalen P., Ezgu F. S., Huledal G., Lindqvist D., Wiken M., ...More

15th Annual Research Meeting of the WORLDSymposium(TM), Florida, United States Of America, 4 - 07 February 2019, vol.126 identifier

  • Publication Type: Conference Paper / Summary Text
  • Volume: 126
  • Doi Number: 10.1016/j.ymgme.2018.12.066
  • City: Florida
  • Country: United States Of America
  • Gazi University Affiliated: Yes