A Phase 3 Trial of Sebelipase Alfa in Lysosomal Acid Lipase Deficiency

---

Copy For Citation

Burton B. K., Balwani M., Feillet F., Baric I., Burrow T. A., Camarena Grande C., ...More

NEW ENGLAND JOURNAL OF MEDICINE, vol.373, no.11, pp.1010-1020, 2015 (SCI-Expanded)

• Publication Type: Article / Article
• Volume: 373 Issue: 11
• Publication Date: 2015
• Doi Number: 10.1056/nejmoa1501365
• Journal Name: NEW ENGLAND JOURNAL OF MEDICINE
• Journal Indexes: Science Citation Index Expanded (SCI-EXPANDED), Scopus
• Page Numbers: pp.1010-1020
• Gazi University Affiliated: Yes

Abstract

BACKGROUND