Early indicators of disease progression in Fabry disease that may indicate the need for disease-specific treatment initiation: findings from the opinion-based PREDICT-FD modified Delphi consensus initiative


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Hughes D. A. , Aguiar P., Deegan P. B. , Ezgu F., Frustaci A., Lidove O., ...Daha Fazla

BMJ OPEN, cilt.10, 2020 (SCI İndekslerine Giren Dergi) identifier identifier identifier

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Objectives The PRoposing Early Disease Indicators for Clinical Tracking in Fabry Disease (PREDICT-FD) initiative aimed to reach consensus among a panel of global experts on early indicators of disease progression that may justify FD-specific treatment initiation.