Early indicators of disease progression in Fabry disease that may indicate the need for disease-specific treatment initiation: findings from the opinion-based PREDICT-FD modified Delphi consensus initiative


Creative Commons License

Hughes D. A. , Aguiar P., Deegan P. B. , Ezgu F., Frustaci A., Lidove O., ...More

BMJ OPEN, vol.10, no.10, 2020 (Journal Indexed in SCI) identifier identifier identifier

  • Publication Type: Article / Article
  • Volume: 10 Issue: 10
  • Publication Date: 2020
  • Doi Number: 10.1136/bmjopen-2019-035182
  • Title of Journal : BMJ OPEN

Abstract

Objectives The PRoposing Early Disease Indicators for Clinical Tracking in Fabry Disease (PREDICT-FD) initiative aimed to reach consensus among a panel of global experts on early indicators of disease progression that may justify FD-specific treatment initiation.