Early indicators of disease progression in Fabry disease that may indicate the need for disease-specific treatment initiation: findings from the opinion-based PREDICT-FD modified Delphi consensus initiative

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Hughes D. A. , Aguiar P., Deegan P. B. , Ezgu F., Frustaci A., Lidove O., ...Daha Fazla

BMJ OPEN, cilt.10, 2020 (SCI İndekslerine Giren Dergi) identifier identifier identifier


Objectives The PRoposing Early Disease Indicators for Clinical Tracking in Fabry Disease (PREDICT-FD) initiative aimed to reach consensus among a panel of global experts on early indicators of disease progression that may justify FD-specific treatment initiation.