Early indicators of disease progression in Fabry disease that may indicate the need for disease-specific treatment initiation: findings from the opinion-based PREDICT-FD modified Delphi consensus initiative

Hughes, Derralynn; Aguiar, Patricio; Deegan, Patrick; Ezgu, Fatih; Frustaci, Andrea; Lidove, Olivier; Linhart, Ales; Lubanda, Jean-Claude; Moon, James; Nicholls, Kathleen; Niu, Dau-Ming; Nowak, Albina; Ramaswami, Uma; Reisin, Ricardo; Rozenfeld, Paula; Schiffmann, Raphael; Svarstad, Einar; Thomas, Mark; Torra, Roser; Vujkovac, Bojan; Warnock, David; West, Michael; Johnson, Jack; Rolfe, Mark; Feriozzi, Sandro

doi:10.1136/bmjopen-2019-035182

Early indicators of disease progression in Fabry disease that may indicate the need for disease-specific treatment initiation: findings from the opinion-based PREDICT-FD modified Delphi consensus initiative

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Hughes D. A. , Aguiar P., Deegan P. B. , Ezgu F., Frustaci A., Lidove O., ...More

BMJ OPEN, vol.10, no.10, 2020 (Journal Indexed in SCI)

Publication Type: Article / Article
Volume: 10 Issue: 10
Publication Date: 2020
Doi Number: 10.1136/bmjopen-2019-035182
Title of Journal : BMJ OPEN

Abstract

Objectives The PRoposing Early Disease Indicators for Clinical Tracking in Fabry Disease (PREDICT-FD) initiative aimed to reach consensus among a panel of global experts on early indicators of disease progression that may justify FD-specific treatment initiation.