Triamterene normalizes glycosaminoglycan accumulation in an IDUA-W402X mouse model of MPS I (Hurler syndrome) via nonsense suppression

Bedwell D., Siddiqui A., Dundar H. , Echols J., Du M., Rasmussen L., ...More

15th Annual Research Meeting of the WORLDSymposium(TM), Florida, United States Of America, 4 - 07 February 2019, vol.126 identifier

  • Publication Type: Conference Paper / Summary Text
  • Volume: 126
  • Doi Number: 10.1016/j.ymgme.2018.12.054
  • City: Florida
  • Country: United States Of America